Genetics
Protocol:VTS-270-303
Condition or Disease: Niemann-Pick Disease, Type C
Study Type: Interventional (Clinical Trial)
Status: Opening Mid 2019
Study Title: An Open-label, Multicenter Safety and Tolerability Study of VTS-270 (2-hydroxypropyl-ë_-cyclodextrin) in Pediatric Subjects Aged < 4 Years With Neurologic Manifestations of Niemann-Pick Type C (NPC) Disease
Principal I investigator: Alan Ikeda, MD
More Info: //clinicaltrials.gov/ct2/show/NCT03687476
