Genetics
Protocol:VTS-270-001
Condition or Disease: Niemann-Pick Disease, Type C
Study Type: Expanded Access
Status: Open for enrollment
Study Title: An Open-label Expanded Access Treatment Protocol for VTS-270 (2-hydroxypropyl-ë_-cyclodextrin) in Patients With Neurologic Manifestations of Niemann-Pick Type C Disease (NPC)
Principal I investigator: Alan Ikeda, MD
More Info: //clinicaltrials.gov/ct2/show/NCT03643562
