Genetics
Protocol:DIREGC07005
Condition or Disease: Pompe
Study Type: Observational
Status: Open for enrollment
Study Title: Pompe Registry
Principal I investigator: Alan Ikeda, MD
More Info: //clinicaltrials.gov/ct2/show/NCT00231400
Blog
Hemophilia Patient Receives FDA Approved Gene Therapy Treatment
Cure 4 The Kids Foundation is the First Facility In Nevada To Administer Transformative Therapy
August 19, 2024
