Genetics
Protocol:DIREGC07006
Condition or Disease: Fabry
Study Type: Observational
Status: Open for enrollment
Study Title: Faby Registry
Principal I investigator: Alan Ikeda, MD
More Info: //clinicaltrials.gov/ct2/show/NCT00196742
Day: January 17, 2019
DIREGC07005 Pompe
Genetics
Protocol:DIREGC07005
Condition or Disease: Pompe
Study Type: Observational
Status: Open for enrollment
Study Title: Pompe Registry
Principal I investigator: Alan Ikeda, MD
More Info: //clinicaltrials.gov/ct2/show/NCT00231400
20101221 Immune Thrombocytopenia
Bleeding and Clotting Disorders
Protocol:20101221
Condition or Disease: Immune Thrombocytopenia
Study Type: Interventional (Clinical Trial)
Status: Closed for enrollment
Study Title: A Single Arm, Open-label, Long-term Efficacy and Safety Study of Romiplostim in Thrombocytopenic Pediatric Subjects With Immune Thrombocytopenia (ITP)
Principal I investigator: Alan Ikeda, MD
More Info: //clinicaltrials.gov/ct2/show/NCT02279173
GENA-99 Hemophilia A
Bleeding and Clotting Disorders
Protocol:GENA-99
Condition or Disease: Hemophilia A
Study Type: Observational
Status: Open for enrollment
Study Title: Prospective, multinational, non-interventional post-authorisation study to document the long-term immunogenicity, safety, and efficacy of Human-cl rhFVIII (simoctocog alfa) in patients with haemophilia A treated in routine clinical practice
Principal I investigator: Joseph Lasky III, MD
More Info: //clinicaltrials.gov/ct2/show/NCT02962765
NN7415-4322 Hemophilia A or B
Bleeding and Clotting Disorders
Protocol:NN7415-4322
Condition or Disease: Hemophilia A or B
Study Type: Observational
Status: Open for enrollment
Study Title: A prospective, multi-national, non-interventional study in haemophilia A and B patients with or without inhibitors treated according to routine clinical treatment practice (explorerâ„¢6)
Principal I investigator: Joseph Lasky III, MD
More Info: //www.clinicaltrials.gov/ct2/show/NCT03741881
